RT Journal Article SR Electronic T1 Global effort against rare and orphan diseases JF European Respiratory Review JO EUROPEAN RESPIRATORY REVIEW FD European Respiratory Society SP 171 OP 172 DO 10.1183/09059180.00004112 VO 21 IS 125 A1 Harari, Sergio A1 Cottin, Vincent A1 Humbert, Marc YR 2012 UL http://err.ersjournals.com/content/21/125/171.abstract AB