Rare pulmonary diseases and orphan drugs: where do we stand and where are we going to?
Sergio Harari, Marc Humbert, Francesco Blasi, Harold R. Collard, Marco Matucci-Cerinic, Gerald Simonneau, Carlo Vancheri, Athol U. Wells, Vincent Cottin
European Respiratory Review Sep 2015, 24 (137) 375-377; DOI: 10.1183/16000617.0051-2015