Cystic fibrosis lung disease starts in the small airways: can we treat it more effectively?

Pediatr Pulmonol. 2010 Feb;45(2):107-17. doi: 10.1002/ppul.21154.

Abstract

The aims of this article are to summarize existing knowledge regarding the pathophysiology of small airways disease in cystic fibrosis (CF), to speculate about additional mechanisms that might play a role, and to consider the available or potential options to treat it. In the first section, we review the evidence provided by pathologic, physiologic, and imaging studies suggesting that obstruction of small airways begins early in life and is progressive. In the second section we discuss how the relationships between CF transmembrane conductance regulator (CFTR), ion transport, the volume of the periciliary liquid layer and airway mucus might lead to defective mucociliary clearance in small airways. In addition, we discuss how chronic endobronchial bacterial infection and a chronic neutrophilic inflammatory response increase the viscosity of CF secretions and exacerbate the clearance problem. Next, we discuss how the mechanical properties of small airways could be altered early in the disease process and how remodeling can contribute to small airways disease. In the final section, we discuss how established therapies impact small airways disease and new directions that may lead to improvement in the treatment of small airways disease. We conclude that there are many reasons to believe that small airways play an important role in the pathophysiology of (early) CF lung disease. Therapy should be aimed to target the small airways more efficiently, especially with drugs that can correct the basic defect at an early stage of disease.

Publication types

  • Review

MeSH terms

  • Administration, Inhalation
  • Airway Obstruction / diagnostic imaging
  • Airway Obstruction / drug therapy
  • Airway Obstruction / physiopathology*
  • Airway Remodeling / drug effects
  • Airway Remodeling / physiology
  • Anti-Inflammatory Agents / administration & dosage
  • Anti-Inflammatory Agents / therapeutic use
  • Child
  • Child, Preschool
  • Cystic Fibrosis / diagnostic imaging
  • Cystic Fibrosis / drug therapy*
  • Cystic Fibrosis / physiopathology
  • Cystic Fibrosis Transmembrane Conductance Regulator / metabolism
  • Cystic Fibrosis Transmembrane Conductance Regulator / physiology
  • Deoxycytosine Nucleotides / administration & dosage
  • Deoxycytosine Nucleotides / therapeutic use
  • Humans
  • Infant
  • Ion Transport / physiology
  • Mannitol / administration & dosage
  • Mannitol / therapeutic use
  • Mucociliary Clearance / drug effects
  • Mucus / diagnostic imaging
  • Mucus / physiology
  • Neutrophils / drug effects
  • Neutrophils / pathology
  • Pneumonia, Bacterial / pathology
  • Pulmonary Alveoli / diagnostic imaging
  • Pulmonary Alveoli / physiology
  • Pulmonary Alveoli / physiopathology*
  • Radiography
  • Respiratory Mucosa / drug effects
  • Respiratory Mucosa / physiopathology
  • Sodium Channel Blockers / administration & dosage
  • Sodium Channel Blockers / therapeutic use
  • Uridine / administration & dosage
  • Uridine / analogs & derivatives
  • Uridine / therapeutic use
  • Young Adult

Substances

  • Anti-Inflammatory Agents
  • CFTR protein, human
  • Deoxycytosine Nucleotides
  • Sodium Channel Blockers
  • Cystic Fibrosis Transmembrane Conductance Regulator
  • Mannitol
  • denufosol tetrasodium
  • Uridine