Treatment of respiratory system (not just lung!) abnormalities in Mucopolysaccharidosis I

J Pediatr. 2004 May;144(5):561-2. doi: 10.1016/j.jpeds.2004.03.002.
No abstract available

Publication types

  • Comment
  • Editorial

MeSH terms

  • Adolescent
  • Humans
  • Iduronidase / adverse effects
  • Iduronidase / therapeutic use*
  • Mucopolysaccharidosis I / complications
  • Mucopolysaccharidosis I / drug therapy*
  • Recombinant Proteins
  • Respiratory Insufficiency / drug therapy*
  • Respiratory Insufficiency / etiology

Substances

  • Recombinant Proteins
  • Iduronidase